Gene therapy

Research News


Gene editing strategy shows promise in mice with spinal muscular atrophy
December 20, 2023 - Dr. Rashmi Kothary’s team played a key role in identifying a new gene-editing strategy that could someday be used to treat spinal muscular atrophy.
Molecule triggered by running could help with stroke recovery
April 18, 2023 - Research suggests that VGF plays a key role in healing the brain after stroke
“Dream team” of researchers tackles leading cause of vision loss
July 27, 2022 - Dr. Catherine Tsilfidis has assembled a world-class team to bring discoveries with game-changing potential to patients with retinal disease
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Researchers


Name Scientific appointment Diseases, conditions and populations of interest Research and clinical approaches
Coutu, Daniel
PhD
Scientist
(Regenerative Medicine)
Aging, Arthritis, Autoimmune disease, Bleeding disorders, Blood cancer, Bone and joint degeneration, Bone and joint injuries, Chronic disease, Musculoskeletal conditions, Osteoporosis 3D printing, Basic research, Bioinformatics, Biomaterials, Cell therapy, Gene expression, Gene therapy, Genetics, Genomics, Imaging, Immunotherapy, Molecular and cellular biology, Proteomics, Regenerative medicine, Stem cells, Surgery, Systems biology, Transgenic/knockout models, Translational research
Diallo, Jean-Simon
PhD
Senior Scientist
(Cancer Therapeutics)
Cancer, COVID-19, Infectious disease Artificial intelligence and data science, Basic research, Cancer biotherapeutics, Cancer immunotherapy, Drug development, Gene therapy, Immunization, Immunotherapy, Molecular and cellular biology, Oncolytic viruses, Translational research, Viral therapy
Gage, Blair
PhD
Scientist
(Regenerative Medicine)
Bleeding disorders, Diabetes, Liver cancer, Liver disease, Vascular, heart and metabolic disease Basic research, Bioinformatics, Cell therapy, Disease models, Gene expression, Gene therapy, Genetics, Genomics, Model organisms, Molecular and cellular biology, Regenerative medicine, Stem cells, Translational research, Transplantation
Ilkow, Carolina
PhD
Senior Scientist
(Cancer Therapeutics)
Breast cancer, COVID-19, Ovarian cancer, Pancreatic cancer Basic research, Cancer biotherapeutics, Cancer immunotherapy, Extracellular vesicles / exosomes, Gene therapy, Immunization, Immunotherapy, Molecular and cellular biology, Oncolytic viruses, Translational research, Viral therapy
Kothary, Rashmi
Ph.D.
Senior Scientist
(Regenerative Medicine)
Neuromuscular disease, Amyotrophic lateral sclerosis, Dystonia, Multiple sclerosis, Muscular dystrophy, Spinal muscular atrophy Basic research, Disease models, Drug development, Epigenetics, Epigenetics, Gene therapy, Genetics, Imaging, Lipidomics, Model organisms, Molecular and cellular biology, Proteomics, Regenerative medicine, Transgenic/knockout models, Translational research
Mei, Shirley
PhD, MSc
Investigator
(Regenerative Medicine)
COVID-19, Septic shock Basic research, Biomarkers, Cell therapy, Critical care, Disease models, Epigenetics, Gene therapy, Knowledge translation and implementation research, Molecular and cellular biology, Regenerative medicine, Stem cells
Parks, Robin
Ph.D.
Senior Scientist
(Regenerative Medicine)
Brain and neuromuscular disease, Cancer, Common cold, Muscular dystrophy, Neuromuscular disease Gene therapy, Molecular and cellular biology, Viral therapy
Quizi, Jennifer
PhD
Investigator
(Cancer Therapeutics)
Cancer, Infectious disease Cancer biotherapeutics, Cancer immunotherapy, Cell therapy, Drug development, Gene therapy, Immunization, Immunotherapy, Molecular and cellular biology, Oncolytic viruses, Translational research, Viral therapy